In late-stage Parkinson’s disease, the drug levodopa becomes less effective in treating symptoms because of the inexorable loss of dopamine-releasing
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Clinical trial using gene therapies for neurodegenerative diseases reports positive interim data
Sio Gene Therapies, a clinical-stage company focused on developing gene therapies for neurodegenerative diseases, presented positive interim data from its
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Specialized cells that keep the heart beating have ability to regenerate after birth, study reveals
Specialized cells that conduct electricity to keep the heart beating have a previously unrecognized ability to regenerate in the days
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Gene causing inherited heart condition identified
A UCL-led research team has identified a new gene as a cause of hypertrophic cardiomyopathy, an inherited heart condition affecting
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More variants of TLR7 gene found in young, healthy men with severe COVID-19
Spanish-Dutch research has revealed two new mutations in the TLR7 gene in healthy young men who became seriously ill with
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Gene therapy breakthrough offers hope to children with rare and fatal brain disease
Scientists and doctors at University College London Great Ormond Street Institute of Child Health (UCL GOS ICH) and Great Ormond
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New components for oligonucleotide drugs show safety, efficacy in treating spinal muscular atrophy
Skoltech researchers and their colleagues from Russia and the UK investigated the safety and efficacy of new chemistry in antisense
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Researchers identify gene responsible for increased risk of infantile fragility
An intrauterine fracture is a rare finding during routine prenatal imaging. This condition can be due to maternal trauma or
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Gene therapy more cost effective than current treatments for hemophilia B
A St. Jude Children’s Research Hospital analysis found a major gap between the cost to manufacture and distribute hemophilia B
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New microbial genes responsible for bile acid conversion is a major step forward for gut health
As the owner of a human body, you're carrying trillions of microbes with you everywhere you go. These microscopic organisms
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