Nearly two decades ago, a gene therapy restored vision to Lancelot, a Briard dog who was born with a blinding
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New method enables more extensive preclinical testing of heart drugs and therapies
Researchers at the University of Louisville have developed an easily reproducible system that enables them to keep slices of human
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Preventing hereditary deafness: Optimized gene-editing tool prevents hearing loss in mice with hereditary deafness without detectable off-target effects
Scientists at Harvard Medical School and Boston Children’s Hospital have used a novel gene-editing approach to salvage the hearing of
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Treatment targeted at a genetic mutation relieves psychosis symptoms: Proof-of-principle findings pave the way for precision medicine in psychiatry
Treatment of psychosis can be targeted to a specific genetic mutation in patients with psychotic disorders, according to a study
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Networks of gene activity control organ development: Evolutionary studies on developmental genetic programs across mammals
For the first time, researchers have decoded the genetic programmes that control the development of major organs in humans and
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What is known — and not known — about heart muscle diseases in children
Cardiomyopathies (heart muscle diseases) in children are the focus of a new scientific statement from the American Heart Association that
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Gene-based factor VIIa prevents bleeding episodes in animals with hemophilia: Preclinical work offers first target levels for bypass agent prophylaxis in future human trials
Hematology researchers have further refined how a treatment currently used on an urgent basis to control bleeding in hemophilia patients
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Famous cancer-fighting gene also protects against birth defects
New research has revealed how the famous tumour suppressor gene p53 is surprisingly critical for development of the neural tube
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Exercise adds up to big brain boosts
Anyone who trains for a marathon knows that individual running workouts add up over time to yield a big improvement
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Researchers identify role sex-biased protein may play in autism
Researchers at the University of New Hampshire are one step closer to helping answer the question of why autism is
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